CRISPR Cas9 gene therapy explained with DNA scissors, hereditary diseases treatment, and designer babies ethical dilemmas ...

Cell and gene therapies are moving towards correcting root causes of diseases. Let's take a look at future cell and gene therapy trends.

Gene therapy represents one of medicine’s most ambitious attempts to treat disease at its root cause by altering the genetic code itself. The approach works by recovering the functions of critical ...

Dr Romain Joubert of AviadoBio explained how the company has used an adeno-associated virus gene replacement programme in ...

With an end-of-week green light from the FDA, Rocket Pharmaceuticals has officially broken into commercial orbit.  | Rocket has announced that the FDA signed off on an accelerated approval for its ...

SEATTLE — Some of our most challenging health conditions result from genetic disorders like sickle cell disease and certain cancers. Gene therapy is revolutionizing how they're treated, and the Fred ...

UF scientist develops safer gene therapy restoring vision in children with rare inherited eye diseases; pivotal trials begin this year.

Upon approval, Rocket has been awarded a priority review voucher, which currently fetch around $200m on the secondary market.

Professor Eric Alton outlined how a 25-year UK collaboration has pushed respiratory gene therapy from concept towards the ...

A phase 1/2 trial of a novel viral vector gene therapy in adults with type 1 diabetes is scheduled to begin this year.

Technologies for the development of new RNA treatments and gene therapy are marking new milestones in Italy, with the ...